Daily function – Critical Path Rare Disease App

Timed Up and Go Test (TUG)

Timed Up and Down Stairs

Revised Upper Limb Module

Rasch-built Pompe-specific activity scale

Revised Hammersmith Scale

Quality of Life in Neurological Disorders Scale v1.1 – Pediatric Upper Extremity – Fine Motor, ADL

Quality of Life in Neurological Disorders Scale v1.1 – Pediatric Lower Extremity

Pediatric Outcome Data Collection Instrument – Parent

Pediatric Outcome Data Collection Instrument – Self-Report

Pediatric Evaluation of Disability Inventory™